Emerging Drug Therapies for Inherited Retinal Dystrophies.

Authors

Husvinee Sundaramurthi, Ailís Moran, Andrea Cerquone Perpetuini, Alison Reynolds, Breandán Kennedy

Published in

Advances in experimental medicine and biology. Volume 1185. Pages 263-267.

Abstract

Worldwide, 1 in 2000 people suffer from inherited retinal dystrophies (IRD). Individuals with IRD typically present with progressive vision loss that ultimately results in blindness. Unfortunately, effective treatment options are not widely available due to the genetic and clinical heterogeneity of these diseases. There are multiple gene, cell, and drug-based therapies in various phases of clinical trials for IRD. This mini-review documents current progress made in drug-based clinical trials for treating IRD.

PMID:
31884622
Bibliographic data and abstract were imported from PubMed on 15 Sep 2025.

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